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You can access this
clinical trial
if you have
Spinal Muscular Atrophy (SMA)
and you are
under 6
years old
Phase
-
This is an observational trial.
You are contributing to medical knowledge about your condition.
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The purpose

Spinal muscular atrophy (SMA) is the leading genetic cause of death of infants. Strong preclinical evidence suggests that effective therapy must be delivered as early as possible to prevent progression of the disease. The primary study objective will be to identify prognostic and surrogate biomarkers of disease progression that will facilitate the execution of therapeutic SMA clinical trials in infants.
Tris trial is registered with FDA with number: NCT01736553. The sponsor of the trial is Ohio State University and it is looking for 53 volunteers for the current phase.
Official trial title:
Spinal Muscular Atrophy (SMA) Biomarkers in the Immediate Postnatal Period of Development