Your journey
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More info
You can access this
clinical trial
if you have
Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency, Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2), Mitochondrial Trifunctional Protein Deficiency, Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency, Glycogen Storage Disorders, Pyruvate Carboxylase Deficiency Disease, ACYL-CoA DEHYDROGENASE FAMILY, MEMBER 9, DEFICIENCY of or Barth Syndrome
and you are
over 1
years old
-
The phase for this study is not defined.
Show me locations

The purpose

This is a compassionate use study to allow patients already taking triheptanoin (C7) through previous studies to continue to receive the supplement. It will also allow triheptanoin supplementation in patients with qualifying disorders if they are failing conventional therapy.

Provided treatments

  • Drug: triheptanoin
Wondering what is the locations section for?
We will connect you to the doctor responsible for this trial and help you get more information.

Locations near you

Unfortunately, there are no recruiting locations near you. Please check the list with all locations below.
Tris trial is registered with FDA with number: NCT01461304. The sponsor of the trial is Jerry Vockley, MD, PhD and it is looking for 0 volunteers for the current phase.
Official trial title:
Dietary Therapy for Inherited Disorders of Energy Metabolism