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Your journey
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More info
You can access this
clinical trial
if you have
Fanconi Anemia
and you are
over 4
years old
1
This is an early phase trial to determine
the dosage and safety of the new treatment.
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The purpose

This clinical trial will access the toxicity and efficacy of infusion of gene modified cells for patients with Fanconi anemia (FA). Infusion of autologous patient blood stem cells that have been corrected in the laboratory by introduction of the normal gene may improve blood counts in patients with FA.

Provided treatments

  • Procedure: Bone Marrow Aspiration
  • Biological: Filgrastim
  • Biological: Genetically Engineered Hematopoietic Stem Progenitor Cells
  • Other: Laboratory Biomarker Analysis
  • Procedure: Leukapheresis
  • Drug: Methylprednisolone
  • Drug: Plerixafor
  • Drug: Prednisone

Locations near you

Unfortunately, there are no recruiting locations near you. Please check the list with all locations below.
Tris trial is registered with FDA with number: NCT01331018. The sponsor of the trial is Fred Hutchinson Cancer Research Center and it is looking for 3 volunteers for the current phase.
Official trial title:
Gene Transfer for Patients With Fanconi Anemia Complementation Group A (FANCA)